Research Summaries

Research Summary
Research Summary
05/08/2026
Anthony Calabro, MA
A phase 3 randomized trial found that Mim8 prophylaxis significantly reduced bleeding rates compared with on-demand therapy and clotting factor prophylaxis in patients with hemophilia A with or without...
05/08/2026
Research Summary
Research Summary
05/01/2026
Ashton L. Stahl
A phase 3 trial evaluated weekly marstacimab prophylaxis in adolescents and adults with hemophilia A or B with inhibitors.
05/01/2026
Research Summary
Research Summary
05/01/2026
Ashton L. Stahl
Final phase 3 results assessed 5-year efficacy and safety of etranacogene dezaparvovec in adults with hemophilia B.
05/01/2026
FDA Alert
FDA Alert
01/09/2025
Anthony Calabro, MA
The FDA has approved concizumab-mtci, a daily subcutaneous treatment to reduce bleeding for patients with hemophilia who have clotting factor inhibitors.
01/09/2025
FDA Alert
FDA Alert
10/25/2024
Miranda Manier, BA
The FDA has approved a novel therapy for patients with hemophilia A or B without inhibitors. Clinical trials showed it significantly reduces bleeding episodes by targeting a new protein in the blood...
10/25/2024
Bleeding Disorders
fda sign
Bleeding Disorders
11/28/2022
The first of its kind gene therapy treatment has been approved by the FDA for adults with Hemophilia B.
11/28/2022
Hematology
Hematology
06/01/2017
The US Food and Drug Administration recently approved a new treatment option for patients with hemophilia B.
06/01/2017